A recent study has shed light on the potential benefits of arimoclomol for individuals with Niemann-Pick disease type C (NPC). This study, known as NPC-002, was a 12-month trial. It was designed to be double-blind and randomized, with a placebo group for comparison. The main goal was to see how arim
The world of clinical trials is changing fast. The focus is now on putting patients first. This means making sure they stay involved, follow the rules, and want to take part. To do this, more trials are using technology to reach patients where they are. This is called decentralized clinical trials o
The meniscus is a crucial part of the knee joint. It acts like a cushion between the thighbone and shinbone. When part of it is removed, it can lead to problems later on. A study looked at how well a polyurethane scaffold helps in the long run. This scaffold is used to fix chronic issues after part
The hunt for volunteers in liver disease studies is tough. Why? Because liver issues like cancer and scarring are complicated. Doctors need to check many details to find the right people. This is usually done by hand, which takes ages and can lead to mistakes. But there's hope on the horizon. Artifi
Afatinib and capecitabine are two drugs that are being tested together in a clinical trial. This trial is for people who have cancers that are hard to treat. These cancers include pancreatic ductal adenocarcinoma, biliary tract cancers, and other solid tumors. The epidermal growth factor re
Bile duct cancer, also known as biliary tract carcinoma, is a tough nut to crack. It is a serious disease that has not seen many breakthroughs in treatment. It is not all doom and gloom, though. Researchers have been testing out different ways to fight this disease. They have been looking at com
In the realm of medical research, there's a lot of talk about a condition known as paroxysmal nocturnal hemoglobinuria. This is a rare blood disorder that can cause red blood cells to break down too quickly. This can lead to anemia, which is when the body doesn't have enough healthy red blood cells
Kidney surgery can be tough on the body. One of the main concerns is protecting the kidney from damage. One way to do this is by using a substance called mannitol. It is often given to patients before the blood flow to the kidney is temporarily stopped during surgery. This is a common step in a
Brain scans using electroencephalography (EEG) have been a hot topic in mental health research. These scans measure electrical activity in the brain and can help spot patterns linked to mental health conditions. One big area of focus is on people at high risk for psychosis. These individuals, often
A condition known as neurofibromatosis type 1 (NF1) can cause tumors to grow along nerves in the body. These tumors, called plexiform neurofibromas, can be particularly troublesome when they are inoperable and cause symptoms. Until now, there have been no approved treatments worldwide for adults dea
