A recent study has shed light on the potential benefits of arimoclomol for individuals with Niemann-Pick disease type C (NPC). This study, known as NPC-002, was a 12-month trial. It was designed to be double-blind and randomized, with a placebo group for comparison. The main goal was to see how arim
The world of clinical trials is changing fast. The focus is now on putting patients first. This means making sure they stay involved, follow the rules, and want to take part. To do this, more trials are using technology to reach patients where they are. This is called decentralized clinical trials o
The hunt for volunteers in liver disease studies is tough. Why? Because liver issues like cancer and scarring are complicated. Doctors need to check many details to find the right people. This is usually done by hand, which takes ages and can lead to mistakes. But there's hope on the horizon. Artifi
Afatinib and capecitabine are two drugs that are being tested together in a clinical trial. This trial is for people who have cancers that are hard to treat. These cancers include pancreatic ductal adenocarcinoma, biliary tract cancers, and other solid tumors. The epidermal growth factor re
Bile duct cancer, also known as biliary tract carcinoma, is a tough nut to crack. It is a serious disease that has not seen many breakthroughs in treatment. It is not all doom and gloom, though. Researchers have been testing out different ways to fight this disease. They have been looking at com
Kidney surgery can be tough on the body. One of the main concerns is protecting the kidney from damage. One way to do this is by using a substance called mannitol. It is often given to patients before the blood flow to the kidney is temporarily stopped during surgery. This is a common step in a
Semaglutide is a game-changer in the fight against type 2 diabetes and obesity. It is a type of drug that mimics natural hormones in the body. This drug is available in two forms: a pill and an injection. Both have shown impressive results in managing weight and blood sugar levels over the long t
Tinnitus is a condition that affects millions of people worldwide. It is often described as a ringing or buzzing sound in the ears. This condition can be quite bothersome. It can disrupt sleep, concentration, and overall quality of life. Traditional treatments have had limited success. However, a ne
Finerenone is a drug that has been tested in various trials. These tests have involved people with heart failure. Two types of heart failure were looked at. One is heart failure with mildly reduced ejection fraction. The other is heart failure with preserved ejection fraction. Both types are serious
Breast cancer affects many people. But when it comes to clinical trials, some groups are missing. Black and Hispanic patients are not as likely to join these trials. This is a problem. It makes it hard to give fair care to everyone. There are reasons for this gap. Understanding these reasons i
